Financial assistance is gratefully acknowledged from:
Bayer
Biomarin Pharmaceutical
Catalyst Biosciences
CSL Behring GmbH
F Hoffmann-La Roche
LFB Biomedicaments
Novo Nordisk Health Care AG
Octapharma AG
Pfizer Limited
Sanofi Genzyme
Sobi
Spark Therapeutics
Takeda Pharmaceuticals International AG
uniQure Inc.